Dravet Gene Therapy Tested in Mice, Sarepta’s Setback, and AstraZeneca Updates

Dravet Gene Therapy Tested in Mice, Sarepta’s Setback, and AstraZeneca Updates

Gene therapies take center stage in this week’s episode. We discuss a potential gene replacement therapy for people with Dravet Syndrome that scientists have tested in mice with good results and highlight some recent progress from two editing companies. We also break down the recent news from Sarepta about the death of a patient after treatment with its gene therapy for Duchenne muscular dystrophy.  In other stories, new data reveals a nonviral …