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Potrebna pomoć maloj Minji, prva u svetu treba da primi gensku terapiju za ADSL

Summary by n1info.rs
Dvogodišnja Minja Lapčević, koja boluje od deficijencije adenilosukcinatne lijaze (ADSL deficijencija) na putu je da bude prvi pacijent u svetu koji je primio gensku terapiju za ovaj izuzetno redak metabolički poremećaj.

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