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Larimar Reports Positive Long-Term Data on Nomlabofusp in Friedreich’s Ataxia
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Larimar Reports Positive Long-Term Data on Nomlabofusp in Friedreich’s Ataxia
BALA CYNWYD, PA — Larimar Therapeutics, Inc. (Nasdaq: LRMR) reported new long-term open-label (OL) data for nomlabofusp in Friedreich’s ataxia (FA), showing sustained increases in frataxin (FXN) protein and consistent directional improvements across four clinical outcomes, alongside a revised starting-dose regimen and an accelerated-approval BLA timeline for Q2 2026. As of August 27, 2025, 39 participants in the OL study had received at least on…
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