I’m a Rare Disease Mom, and I Finally Have New Hope for My Son’s Future

I’m a rare disease mom, and I finally have new hope for my son’s future

The plausible mechanism framework, which the FDA has just released guidance on, offers a new bridge between scientific progress and children who need it.

Rare disease developers applaud clarity in FDA guidance

Several new guidance documents issued by the FDA are poised to significantly impact the rare disease development landscape.The post Rare disease developers applaud clarity in FDA guidance appeared first on Clinical Trials Arena.