First Patient to Receive Gene Therapy 'Cure' for Beta-Thalassemia Living Pain-Free

First Patient to Receive Gene Therapy 'Cure' for Beta-Thalassemia Living Pain-Free

In 2020, GNN reported that CRISPR gene editing technology was being used to develop a medicine for beta-thalassemia, a genetically-inherited blood disorder. Now though, another medicine—a ‘cure’—has already been used to treat a young girl, and more individuals are lined up for treatment. Developed at the Children’s Hospital of Philadelphia (CHOP) and called Zynteglo, the […] The post First Patient to Receive Gene Therapy ‘Cure’ for Beta-Thalasse…