FDA Approves First Treatment for Rare Brain Folate Disorder

FDA Approves First Treatment for Rare Brain Folate Disorder

WASHINGTON, D.C. — The U.S. Food and Drug Administration has approved expanded use of the drug Wellcovorin for patients with a rare genetic neurological disorder, providing the first FDA-approved treatment for cerebral folate deficiency linked to the FOLR1 gene. What This Means for You The FDA approved Wellcovorin for patients with a rare genetic condition affecting folate transport to the brain. The treatment is approved for both adults and ch…