First Personalized Gene Therapy Using Base Editing Shows Promising Results in Baby with Rare Disorder

Gene editing helps baby with rare disease thrive

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him.

Baby in the US becomes the first treated with personalized CRISPR Gene-Editing

In a groundbreaking advancement in genetic medicine, a baby in the United States has become the first person to be treated with a personalized CRISPR gene-editing therapy, marking a historic moment for science and the future of rare disease treatment. According to a report by ScienceAlert, the infant was born with a rare and deadly […]

For the first time, a child with a life-threatening hereditary disease has been treated by surgically precise gene therapy. However, the little "KJ" still has to hope for healing.

For the first time, a futuristic gene therapy has helped a sick baby. The new technique allowed doctors to modify the DNA of a baby...

International researchers have called the treatment a promising medical milestone.

How a custom-made gene therapy could save one baby's life

A baby born with a rare, life-threatening genetic disease is now thriving after receiving an experimental gene-editing treatment. He's one of the first to be successfully treated with a bespoke therapy targeting a tiny but deadly error in his DNA. His doctors hope the technology could one day help the estimated 350 million people worldwide with rare diseases.