What a gene therapy win means for the Huntington’s disease pipeline

What a gene therapy win means for the Huntington’s disease pipeline

Recent results for a Huntington’s gene therapy confer a hopeful sign for R&D in the space.

An end in sight for Huntington's disease?

[Previous: In vivo gene editing: The medicine of the future]It's taken years of diligent work, much frustration, and countless failures, but science is finally unlocking the potential of genetic engineering to cure disease.Our first successes were with blood disorders like sickle-cell, where cells with faulty genes can be extracted and treated in a lab. That was the easiest target, but we've kept progressing, gaining the ability to target more c…